Fierce Pharma

JUNE 22, 2023

After several delays and a narrow advisory committee vote, Sarepta’s Duchenne muscular dystrophy (DMD) gene therapy has finally won an accelerated approval. It's now branded as Elevidys.

Gene Therapy 89

Gene Therapy Gene Branding 89

BioPharma Reporter

JANUARY 13, 2022

Protagen, BioAnalytix, and GeneWerk this week announced their unified operations and re-brand as ProtaGene, a CRO partner for the biologics and cell and gene therapy developers, from discovery to commercialization.

Gene Therapy 126

Gene Therapy Branding Gene Development 126

Pharmaceutical Technology

JUNE 29, 2022

The next wave of medicine is well on course to be cell and gene-based. For cell and gene therapy applications, you need a variety of speciality enzymes of the highest purity, specificity, and consistency. Meanwhile, the pharma industry is undergoing somewhat of a transformation itself. And it’s within the family – Novozymes!”.

Drugs 295

Drugs Gene Therapy Production Manufacturing 295

Pharmaceutical Technology

JULY 26, 2022

NPC is caused by mutations in the NPC1 gene (NPC type 1C) or the NPC2 gene (NPC type 2C) and is inherited in an autosomal recessive manner. Most cases are detected during childhood and progress to cause life-threatening complications by the second or third decade of life.

Marketing 306

Marketing Gene Branding Clinical Development 306

Pharmaceutical Commerce

JULY 3, 2024

The deal provides the CDMO with ownership of the Lexington facility, allowing for late-phase and commercial gene therapy development and manufacturing of a branded severe Hemophilia B product.

Gene Therapy 52

Gene Therapy Gene Branding Manufacturing 52

Pharma Marketing Network

FEBRUARY 27, 2025

Introduction In todays digital-first world, content marketing campaigns are no longer optional for pharmaceutical brands. Imagine content marketing as the heartbeat of a pharma brands digital presence. Instead of traditional promotional tactics, pharma brands can use educational content to build credibility.

Branding 52

Branding Marketing Compliance Pharma Companies 52

STAT News

JANUARY 11, 2023

The company expects its Covid-19 antiviral pill to be launched in the Chinese market on Friday, but noted that Sinopharm is the only legally authorized distributor there of molnupiravir, which is sold under the brand name Lagevrio and was developed by Merck and Ridgeback Biotherapeutics.

Gene Therapy 98

Gene Therapy Licensing Licensing Gene 98

XTalks

MAY 22, 2023

Conscious Greens is the first offering from Pairwise’s new brand, Conscious Foods. Pairwise teamed up with Performance Food Group (PFG) to co-brand its Purple Power Baby Greens Blend under PFG’s Peak Fresh Produce premium brand. Paul region, St. Louis and Springfield, Massachusetts.

Branding 98

Branding Gene Editing DNA Production 98

Pharmaceutical Technology

FEBRUARY 23, 2023

It covers a broad range of techniques from the less invasive practice of intermittent fasting to drastic and invasive procedures, such as the implanting of microchips or injecting of gene-editing enzymes. The biohacking movement in its current branding has been around for more than a decade. How did biohacking start?

Gene Editing 278

Gene Editing Regulation Production Nurses 278

The Pharma Data

MAY 26, 2023

With broad and deep scale and expertise in development sciences, delivery technologies, and multi-modality manufacturing, Catalent is a preferred industry partner for personalized medicines, consumer health brand extensions, and blockbuster drugs.

Clinical Supply 52

Clinical Supply Gene Therapy Gene Development 52

Pharmaceutical Technology

JULY 28, 2022

Avastin, which is currently used as an off-label therapy for wAMD, is also of interest as Outlook Therapeutics is working on developing a branded version for this indication. A one-time treatment option would represent a significant shift in the treatment burden for wAMD.

Marketing 130

Marketing Gene Therapy FDA Approval Development 130

pharmaphorum

APRIL 25, 2022

With iPSCs exhibiting game-changing potential in the bid to develop an off-the-shelf therapy, the brand-new iPSC Manufacturing Summit is the only summit dedicated to solving the manufacturing, quality and analytical challenges hindering your iPSC-derived treatments from reaching patients. Hear from: Fate Therapeutics. Notch Therapeutics.

Manufacturing 52

Manufacturing Gene Editing Branding Production 52

pharmaphorum

MARCH 31, 2021

Novartis has been steadily building itself into a radio-oncology powerhouse in the last few years, seeing the category as one of four pillars of its cancer business, along with cell and gene therapy, targeted drugs and immunotherapeutics. In 2018 it paid $2.1

Licensing 98

Licensing Licensing Gene Therapy Sales 98

pharmaphorum

APRIL 5, 2022

The technique was able to predict individual drug responses more accurately than genetic features, such as mutations in three key genes (EGFR, KRAS and PIK3CA) which are already used to select patients for treatment with targeted drugs.

Protein 67

Protein Genome Genomics Genetic Analysis 67

Pharma Marketing Network

DECEMBER 21, 2020

those that modify the expression of an individual’s genes or repair abnormal genes) has entered clinical practice, including 11 RNA therapeutics, 2 in vivo gene therapies, and 2 gene-modified cell therapies. This relinquishes many of the perceived benefits of RNAi therapies that distinguish them from gene therapy (e.g.,

Genetics 52

Genetics Medicine Gene Therapy Marketing 52

pharmaphorum

AUGUST 19, 2020

Our community of supply chain experts are looking forward to connecting with you in the digital world, including: Christopher Baldwin , Supply Chain Director, Cell & Gene Therapy¸ GSK. Get your copy of the brand-new agenda for the full list of speakers and sessions. Kawa Chiu , VP CMC Supply Chain, Lyell Immunopharma.

Gene Therapy 52

Gene Therapy Packaging Packaging Branding 52

XTalks

JUNE 14, 2023

The exact cost of Vevye has not been publicly disclosed; however, it is estimated that the price of Vevye may be in the range of similar cyclosporine ophthalmic emulsions, such as brand-name Restasis that carries a list price of $645.63 for a 30-day supply (without insurance coverage).

Gene Silencing 97

Gene Silencing Drug Delivery FDA Approval RNA 97

pharmaphorum

MAY 10, 2022

For me, on top of the patient focus, it’s about creating connectivity — bringing your science, data, brand, company at the right moment in the right channel with the right insights to your audience,” Mark Mulder states. That’s a brand-new channel that wasn’t there 10 years ago.

Marketing 98

Marketing Gene Therapy Sales Branding 98

pharmaphorum

MARCH 21, 2022

Eli Lilly is investing $700M into genetic medicine, announcing plans to establish a Boston research center, and with the acquisition of Prevail Therapeutics in late 2020, Lilly secured access to two gene therapies that had already advanced into human testing — with one targeting Parkinson’s disease and the other, dementia.

Genetics 52

Genetics Development Drugs Gene Therapy 52

Drug Channels

JUNE 5, 2023

View the Agenda Snapshot Enhance Patient Service, Network Design, and Channel Strategies to Improve Patient Access and Support In its 8th year, the Specialty Network and Patient Support Services Summit is an important event for senior leaders in patient access, trade, channel, market access, brand and account strategy.

Pharmacy 74

Pharmacy Gene Therapy Manufacturing Compliance 74

pharmaphorum

MARCH 19, 2021

Scientists have identified responsible genes for approximately 50% of the estimated 7000 rare diseases 2. Concentrating on patient identification early in the clinical phases can drive brand loyalty and develop more effective tactics, to address unmet patient needs. How do you find rare disease patients?

Branding 52

Branding Genome Genomics Genetics 52

Pharmaceutical Technology

MAY 23, 2023

In April, the pilot-level Nordic Pharmaceutical Forum (NPF) initiative, representing Finland, Iceland, Norway, Sweden, and Denmark, released an updated strategy document outlining the region’s plans to establish a joint procurement mechanism for medicines, with a declared focus on advanced therapy medicinal products (ATMPs) such as gene therapies.

Medicine 130

Medicine Gene Therapy Marketing Gene 130

The Pharma Data

SEPTEMBER 29, 2021

Data from four distinct analyses for Vitrakvi (larotrectinib) showcase its sustained clinical benefit for patients with solid tumors harboring an NTRK gene fusion (also referred to as TRK fusion cancer). About TRK Fusion Cancer TRK fusion cancer occurs when an NTRK gene fuses with another unrelated gene, producing a chimeric TRK protein.

Gene 52

Gene Protein Clinical Trials Clinical Trials 52

The Pharma Data

MARCH 23, 2021

Berlin, March 23, 2021 – Bayer announced today that the Japanese Ministry of Health, Labor and Welfare (MHLW) has granted marketing authorization for larotrectinib, under the brand name Vitrakvi , for the treatment of Neurotrophic Tyrosine Receptor Kinase ( NTRK ) fusion-positive advanced or recurrent solid tumors.

Genome 52

Genome Genomics Gene Protein 52

pharmaphorum

SEPTEMBER 17, 2021

Havas Life Medicom, ARK and Pharmadoctor top the agency charts AstraZeneca, klarify and Novartis Gene Therapies top the pharma leader board. Among pharma companies and healthcare organisations, the top three companies, taking two Golds each, were AstraZeneca, klarify and Novartis Gene Therapies. Brand promotion. CREATION.co

Gene Therapy 52

Gene Therapy Gene Allergies Life Science 52

pharmaphorum

FEBRUARY 23, 2021

Mandatory RWE was set out for Novartis’ gene therapy for spinal muscular atrophy (SMA) zolgensma (onasemnogene abeparvovec) in February 2021. Leela worked as an advisor to the Department of Health and Social Care on the 2019 Voluntary Scheme for Branded Medicines Pricing and Access (VPAS).

Marketing 90

Marketing Medicine Gene Therapy Drugs 90

Pharma Marketing Network

FEBRUARY 23, 2023

Donna is an expert in brand building and commercialization. She runs Janssen’s Retina Gene initiatives. AI can help us create a market analog as we go into rare space in gene therapy for the first time.” Training AI with CRM sales force data could create a smart bot for brand sites.” – Donna. “As AI could help patients.

Branding 52

Branding Gene Gene Therapy Marketing 52

XTalks

JANUARY 9, 2024

In the US, some of the brand names that levothyroxine is sold under include Synthroid (from AbbVie), Levoxyl (Pfizer) and Tirosint (by Swiss manufacturer IBSA Institut Biochimique). The primary medication used to treat hypothyroidism is levothyroxine, a synthetic form of the thyroid hormone thyroxine (T4).

Hormones 105

Hormones Antibody Trials Production 105

XTalks

APRIL 5, 2024

In Europe, the drug, branded Albrioza, was turned down by the European Medicines Agency (EMA), a decision that Amylyx appealed and lost in October 2023. Biogen and Ionis Pharmaceuticals’ antisense drug Qalsody received FDA accelerated approval in April 2023 , but only for a small subtype of ALS patients with a mutation in the SOD1 gene.

Trials 98

Trials Drugs Marketing FDA Approval 98

XTalks

JANUARY 26, 2024

” Related: Açaí Bowl Brand OAKBERRY Secures $67 Million in Series C Funding Monk Fruit Sweeteners and Beyond Elo Life Systems is set to launch a ground-breaking monk fruit sweetener in 2026. It employs advanced techniques like molecular farming and gene editing. But Elo Life Systems is not just about sweeteners.

Gene Editing 59

Gene Editing Production Development Branding 59

Pharmaceutical Technology

MAY 10, 2023

Vydura is an oral tablet that acts as a calcitonin gene-related peptides (CGRP) receptor antagonist. Vydura is also sold under the brand name Nurtec. During migraines, the trigeminal nerves are activated that cause CGRP to be released.

Drugs 130

Drugs Medicine Branding Gene 130

The Pharma Data

JUNE 7, 2023

Since its launch, we have been able to demonstrate how beneficial the OneBio integrated biologics development solution can be to sponsors, saving them time on managing multiple partners, and handoffs between companies,” said Karen Flynn, Catalent’s Interim President, Division Head for BioModalities (Cell, Gene and Protein Therapies). “By

Manufacturing 40

Manufacturing Development Protein Gene Therapy 40

pharmaphorum

JANUARY 24, 2022

Health Canada has given the drug a green light – under the Sohonos brand – to treat fibrodysplasia ossificans progressiva (FOP), making it the first treatment for the ultra-rare genetic disorder. FOP is caused by a mutation in the gene for ALK2, which is known as ACVR1. billion takeover of Clementia Pharma in 2019.

Drugs 52

Drugs Genetics Marketing Trials 52

pharmaphorum

APRIL 28, 2022

But the company was inspired to re-brand its rare disease business unit as a response to internal ramp-ups that have occurred over the last few years, Helfgott said. Plus, many of these small players are very good at research, not necessarily at developing or commercialising their brands,” he said.

Pharma Companies 59

Pharma Companies Branding Development Marketing 59

pharmaphorum

JUNE 16, 2022

NHS England (NHSE) recognises this, pointing to an agreement with Orchard Therapeutics for Libmeldy (atidarsagene autotemcel), a gene therapy for metachromatic leukodystrophy (MLD) as well as spinal muscular atrophy (SMA) therapy, Zolgensma (onasemnogene abeparvovec).

Medicine 52

Medicine Branding Sales Gene Therapy 52

XTalks

NOVEMBER 1, 2024

It is a biologic drug available exclusively as a brand-name medication, with no generic or biosimilar forms available. Botox is one of the most prescribed branded treatments for chronic migraine prevention, offering rapid relief with just four treatments per year. Price of Zolgensma: Zolgensma has a price of $2.1

FDA Approval 85

FDA Approval Drugs Botox Sales 85

pharmaphorum

JANUARY 4, 2022

Spinraza – which is also an antisense drug originated by Ionis – had the SMA market to itself for a couple of years after its launch in the US in 2017, growing quickly to reach more than $2 billion in 2019 before Novartis’ one-shot gene therapy Zolgensma (onasemnogene abeparvovec) reached the market.

Sales 52

Sales Gene Therapy Marketing Drugs 52