FDA Approves First Drug to Improve Growth in Children with Most Common Form of Dwarfism
The Pharma Data
NOVEMBER 21, 2021
People with achondroplasia have a genetic mutation that causes a certain growth regulation gene called fibroblast growth factor receptor 3 to be overly active, which prevents normal bone growth. 1][2] Some people with achondroplasia may have delayed motor development early on, but cognition is normal.[3] Inheritance is autosomal dominant.[1][2]
Let's personalize your content