Drugs, Gene, Gene Therapy and Genotype - Clinical Research Informer

10 Key Learnings from Successful Cellular and Gene Therapy Trials for Rare Diseases

XTalks

APRIL 24, 2023

Awareness of rare diseases is growing, and with a better understanding of the pathophysiology of many rare diseases, innovative treatment options are emerging, like gene therapies that can treat the root cause of rare genetic diseases and potentially provide long-term symptom relief, or even a definitive cure.

Gene Therapy

Gene Therapy Gene Trials Clinical Trials

Implementing rapid microbial identification in biotherapy manufacturing

Drug Discovery World

FEBRUARY 1, 2024

Microbial control within biopharmaceutical manufacturing is a critical quality control to help ensure drug products are free from viable microorganisms. Regulatory agencies consider genotypic identification to be more reliable than phenotypic methods.

Manufacturing

Manufacturing Genotype Gene Therapy Compliance

Webinar: Environmental monitoring within biotherapeutic production

Drug Discovery World

FEBRUARY 22, 2024

Microbial control within biopharmaceutical manufacturing is a critical quality control to help ensure drug products are free from viable microorganisms. Regulatory agencies consider genotypic identification to be more reliable than phenotypic methods.

Production

Production Genotype Manufacturing Gene Therapy

Webinar: Understand microbial control in biotherapy production

Drug Discovery World

FEBRUARY 15, 2024

Microbial control within biopharmaceutical manufacturing is a critical quality control to help ensure drug products are free from viable microorganisms. Regulatory agencies consider genotypic identification to be more reliable than phenotypic methods.

Production

Production Genotype Manufacturing Gene Therapy

Webinar: The importance of microbial identification in biotherapy manufacturing

Drug Discovery World

FEBRUARY 8, 2024

Microbial control within biopharmaceutical manufacturing is a critical quality control to help ensure drug products are free from viable microorganisms. Regulatory agencies consider genotypic identification to be more reliable than phenotypic methods.

Manufacturing

Manufacturing Genotype Gene Therapy Compliance

Webinar: Enhancing quality control in biotherapy manufacturing

Drug Discovery World

FEBRUARY 1, 2024

Microbial control within biopharmaceutical manufacturing is a critical quality control to help ensure drug products are free from viable microorganisms. Regulatory agencies consider genotypic identification to be more reliable than phenotypic methods.

Manufacturing

Manufacturing Genotype Gene Therapy Compliance

Can genetic data be a magic bullet for drug R&D?

pharmaphorum

JANUARY 24, 2023

Drug development has long been an issue for the pharma industry, due to the expense and the high failure rate of potential treatments. Ben Hargreaves finds that the vast amount of genetic data that exists today could help provide a faster, more targeted way of developing new drug candidates.

Genetics

Genetics Drugs Genome Project Biobanking

Congenital fibrinogen deficiency market forecast to reach $800m across 3MM by 2031

Pharmaceutical Technology

DECEMBER 15, 2022

High interest has sparked across the CFD drug space as more experts are becoming aware of the clinical efficacy and large market opportunity of using HFC products to treat various AFD indications, including surgeries involving massive blood loss and unexpected trauma. While they treat the symptoms of CFD, they are not curative.

Marketing

Marketing Production Genotype Development

Discover how iPSC derived cells can support drug and gene therapy development

Drug Discovery World

FEBRUARY 9, 2024

DDW recently hosted a webinar ‘Discover how iPSC derived cells can be used to support the development of drug and gene therapies’, supported by DefiniGEN. Chris explained that DefiniGEN is a liver cell company focussed on hepatocytes, particularly supporting the drug development industry in producing liver therapies.

Gene Therapy

Gene Therapy Gene Development Drugs

Using iPSC derived cells for the development of drug and gene therapies

Drug Discovery World

SEPTEMBER 12, 2023

In addition, stable cell lines derived from cancers represent a single and karyotypically abnormal genotype. ‘ Discover how iPSC derived cells can be used to support the development of drug and gene therapies’ will take place on 28 September 4PM BST, 5PM CEST, EDT 11AM, PDT 8AM. Register for free here.

Gene Therapy

Gene Therapy Gene Development Drugs

FDA grants approval for bluebird’s Zynteglo to treat beta-thalassemia

Pharmaceutical Technology

AUGUST 18, 2022

The US Food and Drug Administration (FDA) has granted approval for bluebird bio ’s Zynteglo (betibeglogene autotemcel, beti-cel) for the treatment of the underlying genetic cause of beta?thalassemia A custom-made, one-dose gene therapy, Zynteglo is indicated for such patients who need red blood cells (RBCs) transfusions on a regular basis.

Gene Therapy

Gene Therapy Gene Genotype Genetics

Register now to discover how iPSC derived cells support gene therapy development

Drug Discovery World

SEPTEMBER 19, 2023

In addition, stable cell lines derived from cancers represent a single and karyotypically abnormal genotype. ‘ Discover how iPSC derived cells can be used to support the development of drug and gene therapies’ will take place on 28 September 4PM BST, 5PM CEST, EDT 11AM, PDT 8AM. Register for free here.

Gene Therapy

Gene Therapy Gene Development Protein

Bluebird trumpets long-term data from beta-thalassaemia gene therapy

pharmaphorum

DECEMBER 9, 2020

bluebird bio has presented long-term data from its Zinteglo one-time gene therapy for the blood disorder beta-thalassaemia, as the company continues talks with payers in Europe to bring the ultra-pricey treatment to market. The post Bluebird trumpets long-term data from beta-thalassaemia gene therapy appeared first on.

Gene Therapy

Gene Therapy Gene Genotype Marketing

Discover how iPSC derived cells can be used to support the development of drug and gene therapies

Drug Discovery World

AUGUST 25, 2023

Also, stable cell lines derived from cancers represent a single and karyotypically abnormal genotype. Hepatocellular carcinoma-derived cell lines, such as HepG2s, are less proliferative than CHO or HEK cells but remain readily expandable and retain aspects of hepatocyte function.

Gene Therapy

Gene Therapy Gene Development Genotype

Global Roundup: Overland Pharma Launches in China to Provide Access to Breakthrough Therapies

The Pharma Data

DECEMBER 9, 2020

The Chinese biopharmaceutical industry is growing in leaps and bounds, but there is still a huge unmet need when it comes to getting patients access to the breakthrough therapeutic modalities and platforms like RNAi, cell and gene therapy and others. A solution could be at hand with Overland Pharmaceuticals.

In-Vivo

In-Vivo In-Vitro Antibody Development

How can iPSC derived cells can be used to support drug development?

Drug Discovery World

SEPTEMBER 5, 2023

In addition, stable cell lines derived from cancers represent a single and karyotypically abnormal genotype. ‘ Discover how iPSC derived cells can be used to support the development of drug and gene therapies’ will take place on 28 September 4PM BST, 5PM CEST, EDT 11AM, PDT 8AM. Register for free here.

Development

Development Drugs Protein Genotype

Last chance: Discover how iPSC derived cells support drug development

Drug Discovery World

SEPTEMBER 26, 2023

In addition, stable cell lines derived from cancers represent a single and karyotypically abnormal genotype. ‘ Discover how iPSC derived cells can be used to support the development of drug and gene therapies’ will take place on 28 September 4PM BST, 5PM CEST, EDT 11AM, PDT 8AM. Register for free here.

Development

Development Drugs Protein Genotype

Clinical Research Informer

10 Key Learnings from Successful Cellular and Gene Therapy Trials for Rare Diseases

Implementing rapid microbial identification in biotherapy manufacturing

Trending Sources

Webinar: Environmental monitoring within biotherapeutic production

Webinar: Understand microbial control in biotherapy production

Webinar: The importance of microbial identification in biotherapy manufacturing

Webinar: Enhancing quality control in biotherapy manufacturing

Can genetic data be a magic bullet for drug R&D?

Congenital fibrinogen deficiency market forecast to reach $800m across 3MM by 2031

Discover how iPSC derived cells can support drug and gene therapy development

Using iPSC derived cells for the development of drug and gene therapies

FDA grants approval for bluebird’s Zynteglo to treat beta-thalassemia

Register now to discover how iPSC derived cells support gene therapy development

Bluebird trumpets long-term data from beta-thalassaemia gene therapy

Discover how iPSC derived cells can be used to support the development of drug and gene therapies

Global Roundup: Overland Pharma Launches in China to Provide Access to Breakthrough Therapies

How can iPSC derived cells can be used to support drug development?

Last chance: Discover how iPSC derived cells support drug development

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