XTalks

JANUARY 3, 2025

For the first time in the US, adults living with familial chylomicronemia syndrome (FCS) have an FDA-approved treatment option. The approval of Tryngolza was based on positive results from the Phase III Balance trial, which showed reductions in triglyceride levels and acute pancreatitis events.

FDA Approval 59

FDA Approval Drugs Clinical Trials Clinical Trials 59

World of DTC Marketing

JANUARY 24, 2022

To them, a big payday is a small biotech firm being acquired by a big ten pharma company. When they tell small biotech companies to cut costs, there will often be a significant delay in getting the drug to market or massive layoffs of needed staff. Venture capitalists often don’t look that far forward.

Life Science 225

Life Science Drugs Development Genetic Disease 225

pharmaphorum

JANUARY 10, 2022

Not only this, the potential for this type of therapy extends far beyond infectious diseases and into numerous therapy areas. On the back of the approvals for Pfizer/BioNTech and Moderna, suddenly there is a large amount of interest from big pharma companies to get involved in the mRNA space. Attracting attention.

RNA 111

RNA Vaccine Vaccination Pharma Companies 111

XTalks

DECEMBER 22, 2021

To develop these novel RNA-based therapeutics, we saw a number of big pharma companies team up with smaller biotechs focused on developing RNA-based therapeutics. Non-invasive or minimally invasive medical devices that can diagnose, monitor and treat disease is entering a promising era, and will be a key life science trend next year.

Life Science 98

Life Science RNA Vaccine Vaccination 98

XTalks

DECEMBER 29, 2022

As of December 16, 2022, there are seven US Food and Drug Administration (FDA) approved gene therapies. In 2022 alone, the US regulator approved four new gene therapies, showing the high interest in getting these therapies to market. In 2023, a number of gene therapies are expected to get the FDA green light.

Life Science 52

Life Science Gene Therapy Gene Manufacturing 52

XTalks

JANUARY 6, 2025

Notably, the ASO drug Vitravene (fomivirsen) received US Food and Drug Administration (FDA) approval for treating cytomegalovirus (CMV) retinitis in AIDS patients. Additionally, CRISPR genome-wide screening holds great potential for identifying key disease-associated genes and uncovering novel therapeutic targets.

Gene Therapy 111

Gene Therapy RNA Gene Editing Gene 111