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?5 Things You Need to Know from Our Recent Gene Therapy Webinar

Worldwide Clinical Trials

At the end of May, we hosted a webinar titled “ Changing Times, Changing Therapies: Keeping Up with Advancements in Cell and Gene Therapies ” to provide a quick update on the latest advancements and ongoing in development of these advanced therapeutics. Around 40% of clinical holds are for gene therapy programs.

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Vyjuvek Gets FDA Nod as First Topical Gene Therapy for Rare Skin Disease

XTalks

Krystal Biotech’s Vyjuvek has been awarded US Food and Drug Administration (FDA) approval to make it the first topical gene therapy for the treatment of wounds in patients with the rare, often debilitating skin disease dystrophic epidermolysis bullosa (DEB). As a topical treatment, it is also the first readily redosable gene therapy.

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Vertex and CRISPR Therapeutics submit BLAs to FDA for exa-cel

Pharmaceutical Technology

We want to thank the clinical trial participants and the sickle cell and beta thalassemia communities, as well as the physicians, nurses, coordinators, caregivers and friends who support them.” Cell & Gene Therapy coverage on Pharmaceutical Technology is supported by Cytiva.

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Clinical Research Nurse Finds Opportunities via LinkedIn: We Discuss Gene Therapy, Career Growth!

Clinical Trial Gurus

Clinical research nurses have the background and the experience to virtually demand a great amount of interest from prospective employers. In this video I interview Michele Blue, a research nurse from an academic medical center (AMC). We discuss her career, job prospects, and a lot of other topics related to clinical research.

Nurses 52
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STAT+: A young boy’s nightmare diagnosis, and the $3 million one-time treatment that will likely save his life

STAT News

When the long-awaited moment arrived, a nurse helped Adam Hess loosen a tiny plastic clamp on an intravenous line leading to the chest of his son, who lay asleep in a bed at Boston Children’s Hospital. They had been modified in a lab by adding a functional gene to compensate for a defective one.

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One Minute Summary of May 2024 Patient Forum

WCG Clinical

I’m actually a second career nurse. I am in the Doctorate in Nursing Practice program at the University of California, San Francisco, and I’m really looking forward to, becoming the first person in my family on either side to achieve a doctorate degree. He was three and a half at the time.

Nurses 52
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Novartis hails digital strategy as profits hold up during pandemic

pharmaphorum

In China, Novartis has been working with the internet multinational Tencent on an AI-enabled “digital nurse” to manage heart disease. Sales of spinal muscular atrophy gene therapy Zolgensma have been hit because it requires a course of drugs to suppress the immune system before prescription.

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