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Researchers show novel device improves blood sugar control in hyperinsulinism patients whose pancreas has been removed

Scienmag

Philadelphia, September 13, 2021—Researchers at Children’s Hospital of Philadelphia (CHOP) have demonstrated that an experimental device can improve blood sugar control in patients who developed diabetes after their pancreas was removed to treat their hyperinsulinism, a genetic disease in which the pancreas produces too much insulin.

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Vykat XR Approved as First Treatment for Excessive Appetite in Prader-Willi Syndrome

XTalks

In the pancreas, potassium channels regulate insulin secretion. Related: On Rare Disease Day 2025, We Need More Than You Can Imagine Today marks a historic day for the PWS community. Until now, there have been no FDA-approved treatments addressing this hallmark symptom.

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Surrogate Endpoints: How to Choose the Best One for Your Rare Disease Trial

XTalks

For the following 15 rare diseases, all prevalence (approximate), symptom, etiology and treatment information was taken from the National Organization for Rare Disorders’ (NORD) Rare Disease Database , unless a link to another source is provided. Cushing’s Disease. Acromegaly. Prevalence: 50 to 70 people per 1 million.

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