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FDA Approval of Sanofi’s Enzyme Replacement Drug for ASMD + Disney Actress Partners with Medtronic for Diabetes Tech Campaign – Xtalks Life Science Podcast Ep. 77

XTalks

Hear more about the rare, fatal disease and the new drug approval for it. Ayesha also talked about Medtronic’s new partnership with former Disney star Jennifer Stone on a new ad campaign for its diabetes tech, including the smart insulin injector InPen. Subscribe to the Xtalks Life Science Podcast to never miss a new episode.

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Vykat XR Approved as First Treatment for Excessive Appetite in Prader-Willi Syndrome

XTalks

In the pancreas, potassium channels regulate insulin secretion. Related: On Rare Disease Day 2025, We Need More Than You Can Imagine Today marks a historic day for the PWS community. Until now, there have been no FDA-approved treatments addressing this hallmark symptom.

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Surrogate Endpoints: How to Choose the Best One for Your Rare Disease Trial

XTalks

Acromegaly Surrogate Endpoint: Serum growth hormone and serum insulin-like growth factor 1 (IGF-1) are acceptable surrogate endpoints for acromegaly clinical trials involving somatostatin analogs such as octreotide, lanreotide and pasireotide. Also known as Berardinelli-Seip syndrome, there are four subtypes of lipodystrophy.

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