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Researchers reverse the in vitro and in vivo effects of the mutation that causes Stormorken syndrome

Medical Xpress

They study gene variation and mutations that cause rare genetic diseases. A mutation is a permanent change in the genetic material. That was the case when Thilini Gamage was to carry out one of the studies in her doctoral work with Professor Eirik Frengen at the Institute of Clinical Medicine, University of Oslo.

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High risk, high reward – the future of CAR-T therapy in CLL

Pharmaceutical Technology

Autologous CAR-T therapy does not easily lend itself to treating CLL, as it relies on extracting functional T-cells from the patient’s blood and genetically modifying them in vitro. From a clinical perspective, CAR-T therapy may not be appropriate for patients who are typically eligible for cell therapies.

In-Vitro 279
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Reaction Biology to acquire Vyant Bio subsidiary’s operations in US

Pharmaceutical Technology

The staff in the US from the acquired business will be retained by Reaction to set up its presence in Hershey, which comprises in vitro and in vivo expertise. The staff in the US from the acquired business will be retained by Reaction to set up its presence in Hershey, which comprises in vitro and in vivo expertise.

In-Vivo 130
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CDER regulatory science division touts 2020 accomplishments

The Pharma Data

The division served as the rapporteur in the effort to update the International Council for Harmonisation (ICH) E14 and S7B guidelines on the clinical and nonclinical evaluation of QT/QTc interval prolongation and proarrhythmic potential and leads research for the Comprehensive in vitro Proarrhythmia Assay initiative.

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INVO Bioscience Forms Scientific Advisory Board with Leaders from Fertility Industry

The Pharma Data

Dr. Anderson has been an early adopter in blastocyst embryo transfer, cryopreservation and pioneered blastocyst biopsy with and without laser technology for genetic testing. . SARASOTA, Fla. , 18, 2020 /PRNewswire/ — INVO Bioscience , Inc. Drs. and across the world.

In-Vivo 52
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Angelman Syndrome Market: Insights Into The Recent Late-Stage Drug Failures And Novel Approaches To Treating This Rare Neurogenetic Disorder

Delveinsight

Angelman syndrome (AS) is a complex genetic rare disorder that affects the nervous system. Preclinical studies undertaken to evaluate the drug have shown that GTX-102 activates the paternal copy of the UBE3A gene in neurons in vitro, and can ease certain disease symptoms in a mouse model of Angelman syndrome.

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Transitioning Between Academia and Industry: Advice from Leading Scientists That Made the Switch

XTalks

Leaving academia for industry is a route that academic scientists and professors did not traditionally pursue in the past due to perceived differences in skillsets, experiences and even associated stigmas. However, this has since changed, and now, transitioning between academia and industry has become more commonplace. Key Moments.