XTalks

MARCH 28, 2024

Duvyzat, a histone deacetylase (HDAC) inhibitor that works to reduce inflammation and muscle loss, is the first nonsteroidal drug approved to treat patients with all genetic variants of DMD. Progressive muscle weakness in the disease is caused by genetic mutations in the dystrophin gene that lead to a lack of functional dystrophin protein.

FDA Approval 105

FDA Approval Genetics Gene Therapy Gene 105

Pharmaceutical Technology

FEBRUARY 13, 2023

Gene therapies are an attractive way of targeting the underlying genetic mutations, but traditional approaches cannot be used while targeting mutations for Dravet Syndrome, forcing researchers to develop new ways. In October 2022, mjn-neuro signed a commercialization agreement with the pharma company Neuraxpharm Group to market mjn-SERAS.

Research 264

Research Gene Gene Therapy Genomics 264

World of DTC Marketing

JANUARY 1, 2022

3hree: Pharma will increase its spending in digital, but a lot of the money will be wasted. Studies show that tens of millions of dollars are being wasted due to fraud with programmatic advertising, but many pharma companies are still wasting money on the channel. Invest in product websites with content and usability studies.

Marketing 244

Marketing Doctor Doctors FDA Approval 244

Pharmaceutical Technology

MAY 24, 2023

The ability to modify or introduce genetic material in human cells in such a precise and patient-centered manner clearly constitutes a breakthrough in personalized medicine. CGT drugs fall into two major categories: autologous and allogeneic.

Clinical Trials 246

Clinical Trials Clinical Trials Gene Therapy Clinical Supply Chain 246

World of DTC Marketing

JANUARY 24, 2022

To them, a big payday is a small biotech firm being acquired by a big ten pharma company. When they tell small biotech companies to cut costs, there will often be a significant delay in getting the drug to market or massive layoffs of needed staff. Venture capitalists often don’t look that far forward.

Life Science 225

Life Science Drugs Development Genetic Disease 225

XTalks

JANUARY 20, 2025

This strategic move transformed Actavis into one of the largest pharma companies globally, with a strong presence across branded, generic and over-the-counter (OTC) medicines. The deal was the largest ever by a pharmaceutical company headquartered in Japan and significantly expanded Takedas footprint in the US and European markets.

Marketing 104

Marketing Botox Life Science Pharma Companies 104

Delveinsight

SEPTEMBER 3, 2021

The post Charcot-Marie-Tooth Disease Market Size Expects Growth Owing to Increasing Prevalence, Influx of Pharma Companies and Novel Therapies appeared first on DelveInsight Business Research.

Pharma Companies 52

Pharma Companies Marketing Clinical Trials Clinical Trials 52

World of DTC Marketing

JANUARY 31, 2021

The venture capitalists funding them are looking for a big payday when a pharma company acquires them. I have been recruited by these companies who promise huge payouts when they are acquired if their drug shows promise in clinical trials. In pharma R&D returns have declined to 1.8 percent—a slight decrease of 0.1

In-Vivo 187

In-Vivo Generic Drugs Drugs Gene Therapy 187

pharmaphorum

FEBRUARY 11, 2022

Ipsen has started exclusive negotiations that could see its global consumer health business sold to fellow French pharma company Mayoly Spindler later this year. billion takeover of Clementia Pharma in 2019. billion of its revenues last year.

Sales 103

Sales Pharma Companies Branding Cosmetics 103

pharmaphorum

FEBRUARY 23, 2022

The Japanese drugmaker will get access to Code Bio’s 3DNA non-viral genetic medicine delivery platform, initially for a liver-directed programme, and is also interested in deploying the technology for central nervous system disorders.

Gene Therapy 105

Gene Therapy Gene Gene Sequencing Immune Response 105

pharmaphorum

NOVEMBER 1, 2021

Delytact (teserpaturev) is a genetically engineered oncolytic herpes simplex virus type 1 (HSV-1) that was approved for marketing in Japan earlier this year, and received pricing approval in August at 1.43 million yen (around $12,500) per dose, according to a Pharma Japan report.

Genetic Engineering 122

Genetic Engineering Clinical Trials Clinical Trials Trials 122

pharmaphorum

NOVEMBER 27, 2022

A group representing pharma companies selling precision therapies for cancer has called for a change to the way genomic testing is done in Scotland, to make sure patients get access to targeted drugs. Let’s lead by doing things – by making decisions to lead.”

Genome 104

Genome Genomics Genetics Medicine 104

pharmaphorum

FEBRUARY 16, 2021

UK biotech Exscientia has signed a string of partnerships with pharma companies and other research-based organisations to apply its AI-based drug discovery platform. It is vital that we develop treatments that target neuroinflammatory mechanisms underlying dementia.”.

Research 119

Research Drugs Protein Development 119

pharmaphorum

JANUARY 6, 2021

Pharma companies are always talking about moving ‘beyond the pill’, and Pfizer’s new brand identity embodies that – it’s decades old pill-like logo has been replaced with a DNA double helix that it says reflects its commitment to breakthrough science. — Tinglong Dai (@TinglongDai) January 5, 2021.

DNA 116

DNA Branding Vaccination Vaccine 116

pharmaphorum

MAY 4, 2022

Once selected, Quris can in-license them, progress them through to phase 1 trials and, those that succeed, can be licensed to pharma companies. Once the initial drug candidate is licensed to a pharma company, the profits are then shared with the academic institution or biotech from which Quris originally licensed the drug.

Drugs 143

Drugs Licensing Licensing Pharma Companies 143

pharmaphorum

SEPTEMBER 18, 2020

But although it was dubbed a “dangerous game”, some companies came out on top… On 6th April 1999, two companies with similar science-based cultures and a shared vision of the pharmaceutical industry came together to form what’s now considered as one of the top ten pharma companies in the world: AstraZeneca.

Pharma Companies 116

Pharma Companies Sales Vaccine Vaccination 116

Pharma Marketing Network

JANUARY 29, 2025

Personalized medicine is revolutionizing pharma marketing by tailoring treatments to individual genetic profiles, lifestyles, and medical histories. Leading companies like Roche and Bristol Myers Squibb leverage precision medicine to refine drug marketing efforts. Why is personalized medicine important for pharma marketing?

Marketing 52

Marketing Compliance Big Data Branding 52

pharmaphorum

JANUARY 10, 2022

On the back of the approvals for Pfizer/BioNTech and Moderna, suddenly there is a large amount of interest from big pharma companies to get involved in the mRNA space. This not only allowed Pfizer to establish a COVID-19 vaccine but the company also recently announced that it had begun a study testing an mRNA flu vaccine.

RNA 111

RNA Vaccine Vaccination Pharma Companies 111

pharmaphorum

FEBRUARY 17, 2021

One group excelling in this space is the Genetic Alliance. Their work ranges from developing new services in partnership with the National Health Service (NHS) to working with the All Party Parliamentary Group on Rare, Genetic and Undiagnosed Conditions, and the Department of Health on the UK Strategy for Rare Diseases.

Life Science 98

Life Science Genetics Branding Trials 98

XTalks

DECEMBER 13, 2023

Now, let’s delve into the list of the top ten fastest growing biotech companies in 2023, ranked by their compound annual growth rate (CAGR). These companies were identified through The Americas’ Fastest-Growing Companies 2023 list by the Financial Times.

Genetics 111

Genetics Vaccination Vaccine DNA 111

pharmaphorum

NOVEMBER 30, 2020

“Our belief is that patients should understand the challenges associated with drug development and how those challenges impact them personally… It is emotionally challenging for patients who must put their faith in the hands of pharma companies”.

Gene Therapy 105

Gene Therapy Gene Antibody Clinical Trials 105

XTalks

AUGUST 21, 2023

This attachment halts the advancement of the genetic disorder through a reduction in the formation of fresh, abnormal bone growth. The active ingredient in Sohonos, palovarotene, functions as an agonist of the retinoic acid receptor gamma, which is present in cells that are involved in bone formation.

Drugs 98

Drugs FDA Approval Genetics Clinical Trials 98

pharmaphorum

JUNE 14, 2022

The innovation that is happening within the Chinese biopharma ecosystem means that frequently Western pharma companies are looking to partner with Chinese firms to bring treatments to the US and Europe. Only last month , the US company Merck agreed to pay a potential $1.4

Clinical Trials 98

Clinical Trials Clinical Trials Trials Development 98

XTalks

JANUARY 3, 2025

FCS is a rare genetic disorder that prevents the body from properly breaking down triglycerides (a type of fat in the blood), leading to dangerously high levels. This can result in acute pancreatitis (inflammation of the pancreas), a life-threatening condition causing severe abdominal pain and other health complications.

FDA Approval 59

FDA Approval Drugs Clinical Trials Clinical Trials 59

XTalks

DECEMBER 20, 2023

In 2024, pharma companies and emerging biotechs will improve candidate safety profiles and reduce off-target effects by exploiting predictive intelligence unlocked by AI,” she predicts. These companies are at various stages of research and clinical trials.

Life Science 119

Life Science Gene Editing Development Clinical Trials 119

Cloudbyz

SEPTEMBER 25, 2020

Time is also of the essence in drug development, as competitive product-to-market lead times help pharma companies improve profitability. With the help of artificial intelligence (AI) and individual genetic data, the software predicts the potential effects drugs have on specific genetic markers.

Pharma Companies 52

Pharma Companies Big Data Drugs Clinical Trials 52

pharmaphorum

JANUARY 29, 2021

Since Macrae joined the company just four years ago, Sangamo has more than tripled its staff and raised $1.6 It has also built its own manufacturing site and launched partnerships with six big pharma companies. And ultimately we will be able to add genetic influences to diseases that don’t have a genetic cause.

Gene Editing 145

Gene Editing Gene Gene Therapy In-Vivo 145

pharmaphorum

AUGUST 23, 2021

The vaccine may be a latecomer to the COVID-19 vaccine arsenal, but its approval signals the potential of DNA vaccines and is a boost to companies working in this space. The company also says that it can update the vaccine very easily to deal with mutations in the virus.

DNA 98

DNA Vaccine Vaccination Genetic Engineering 98

Pharma Marketing Network

OCTOBER 17, 2024

Moreover, the adoption of digital tools like mobile apps and telemedicine platforms is facilitating direct communication between pharma companies and end-users. As patients become more digitally savvy, pharma companies are investing in creating seamless digital experiences that cater to their needs and preferences.

Marketing 52

Marketing Pharma Companies Regulation Production 52

XTalks

NOVEMBER 16, 2021

Over a span of more than two decades, de Vries worked with “the largest pharma companies, small biotechs and medical device companies across tens-of-thousands of clinical trials,” according to Medidata.

Life Science 98

Life Science Clinical Research Pharma Companies Engineer 98

pharmaphorum

DECEMBER 21, 2020

As it’s just a messenger molecule, it does not affect the body’s own genetic code when it is injected as a vaccine – but what it does do is instruct cells to code for copies of a certain protein. Their technology is based on synthetic messenger RNA – short for ribose nucleic acid – which is a short transcript of a longer DNA code.

Vaccine 111

Vaccine Vaccination Doctor Doctors 111

pharmaphorum

DECEMBER 16, 2020

Episode four of Kantar Health’s Health Heroes podcast tackles pharma’s rare disease challenges, the role of patient registries and hears a moving story about the rare genetic disorder Tay-Sachs disease. The podcast finishes up with an overview from Geneviève on the current outlook for rare diseases.

Life Science 52

Life Science Pharma Companies Genetics Research 52

XTalks

MARCH 20, 2025

In January 2025, Regeneron, along with Illumina and 17 US health systems, invested $320 million in Truveta , aiming to create the worlds largest genetic database. The company has also been featured multiple times on Fortunes 100 Best Companies to Work For list. Regenerons contribution was $119.5

Sales 59

Sales Production Drugs Development 59

pharmaphorum

SEPTEMBER 7, 2022

The industry may need to carry out behavioural studies to better understand how to recruit and involve these populations, as it is crucial to understand the genetic differences between demographics. The same is true for Asian and Hispanic populations.

Clinical Trials 98

Clinical Trials Clinical Trials Trials Genetics 98

pharmaphorum

AUGUST 10, 2020

This research also shows the complex system that drives our health outcomes, including the environment, our genetics and our social circumstances. Personalisation : creating interventions based on individuals knowing their genetics, biology and psychology as well as their social and geographical environment.

Genetics 124

Genetics Drug Delivery Research Pharma Companies 124

pharmaphorum

SEPTEMBER 11, 2020

Analysts at Pharma Intelligence decided to find out, surveying professionals involved in clinical data management. Their pool of 155 respondents comes from large pharma companies, biotech companies, device developers, and contract research organisations worldwide. What does this mean for clinical trials?

Trials 98

Trials Clinical Trials Clinical Trials Pharma Companies 98

pharmaphorum

JANUARY 3, 2023

For example, patients could sell anonymised access to their medical records, including genetic information, personality traits, and disease status to facilitate research. In the context of DS, it can be achieved by allowing users to sell access to their data to other users who are willing to pay for it. Challenges. Conclusion.

Compliance 105

Compliance Regulation Pharma Companies Genetics 105